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トランスサイレチンアミロイドーシス転帰調査(THAOS)

基本情報

NCT ID
NCT00628745
ステータス
完了
試験のフェーズ
-
試験タイプ
観察
目標被験者数
6,718
治験依頼者名
Pfizer

概要

THAOS is a global, multi-center, longitudinal observational survey open to all patients with transthyretin amyloidosis (ATTR), including ATTR-PN (polyneuropathy), ATTR-CM (cardiomyopathy) and wild-type ATTR-CM. It is open-ended with a minimum duration of 10 years. Patients will be followed as long as they are able to participate. The principal aims of this outcome survey are to better understand and characterize the natural history of the disease by studying a large and heterogenous patient population. Survey data may be used to develop new treatment guidelines and recommendations, and to inform and educate clinicians about the management of this disease.

対象疾患

Transthyretin Gene MutationsTransthyretin Amyloidosis

介入

None. Observational Study.(OTHER)

依頼者(Sponsor)

実施施設 (3)

Kumamoto University

Kumamoto, Japan

Shinshu University School of Medicine

Matsumoto, JP, Japan

千葉大学医学部附属病院

Chiba, Japan